Aiuti Alessandro Professore ordinarioMedicineMEDS-20/A - Pediatria generale e specialistica

Alessandro Aiuti is Deputy Director Clinical Research of the San Raffaele Telethon Institute for Gene Therapy (SR-Tiget) and Head of the Pediatric Immunohematology Unit at IRCCS San Raffaele Hospital in Milan. He is also Full Professor of Pediatrics and Director of the Postgraduate School in Pediatrics at Vita-Salute San Raffaele University.

After graduating in Medicine and Surgery from the University “La Sapienza” of Rome in 1990 and earned a PhD in Human Biology in 1996, he completed postdoctoral training at Harvard Medical School in Boston, focusing on hematopoietic stem cells. His research has made major contributions to the field of gene therapy for rare genetic diseases of the immune system (ADA-SCID, WAS) and lysosomal storage disorders (MLD, MPS1).

Professor Aiuti’s pioneering work led to the first successful gene therapy for ADA-SCID, MLD and WAS, resulting in the European approval of the drug Strimvelis in 2016, Libmeldy in 2020 and Waskyra in 2025. He has authored over 300 publications in top-tier journals, including Nature Medicine, Science, The Lancet, and The New England Journal of Medicine.

He has received numerous awards, such as the 2020 Else Kröner Fresenius Foundation Award.